Nonclinical evaluation of safety of gene therapy drug AAV5 lipoprotein lipase variant (GC304) in the nervous system
LI Qianqian, XIA Yan, HOU Tiantian, WANG Chao, SHI Xixi, MA Xuemei, LIU Ziyang, ZHANG Yingli, WU Xiaobing, WANG Sanlong, LIU Guoqing, GENG Xingchao
Chinese Journal of Pharmacovigilance . 2023, (1): 34 -39 .  DOI: 10.19803/j.1672-8629.20220587